Chaperone therapy for Krabbe disease: potential for late-onset GALC mutations
Nature.com Correspondence: Professor N Sakai, Department of Pediatrics, Osaka University Graduate School of Medicine, 2-2 Yamada-oka, Suita, 565-0871, Osaka, Japan. E-mail: norio@ped.med.osaka-u.ac.jp. 7Current address: Genetic Division, Department of … |